Health Jun 22 First gene therapy for deadly form of muscular dystrophy gets FDA approval for young children By Matthew Perrone, Associated Press
Health Sep 20 After fierce debate, FDA approves first drug for rare form of muscular dystrophy The FDA, reacting to lobbying by patients and families, has approved a drug for Duchenne muscular dystrophy, a rare and lethal disease. By Liz Szabo, Kaiser Health News